Archive for June, 2010
Quinazoline Program Makes Progress Toward Drug Treatment for Spinal Muscular Atrophy — Families of SMA 2010 Program Update
ELK GROVE VILLAGE, IL, Jun 25, 2010 (MARKETWIRE via COMTEX) — Late last year, Families of Spinal Muscular Atrophy (FSMA) announced that it had entered into a groundbreaking exclusive license agreement with Repligen Corporation for the development of a potential treatment for Spinal Muscular Atrophy (SMA). FSMA is dedicated to creating a treatment and cure [...]
In: SMA Research News
Families of Spinal Muscular Atrophy Collaboration With Nationwide Children’s for Gene Therapy Development
Program Update 2010: Families of Spinal Muscular Atrophy (FSMA) Recently Awarded a Grant to the Nationwide Children’s Hospital at Ohio State University Toward Their Gene Therapy Development Program. This Program Works Toward Replacement of the Entire SMN1 Gene, and Has the Potential to Be Groundbreaking in the Treatment of SMA Patients ELK GROVE VILLAGE, IL–(Marketwire [...]
In: SMA Research News
Families of Spinal Muscular Atrophy and California Stem Cell, Inc. Motor GraftTM Project 2010 Update
Families of Spinal Muscular Atrophy (FSMA) has funded $2 Million to date for development of a Cellular Therapy for SMA. In collaboration with California Stem Cell, Inc. (CSC), we have completed an important, formal pre-Investigational New Drug (Pre-IND) meeting with the Food and Drug Administration (FDA) for guidance on the clinical and regulatory pathway and requirements [...]
In: SMA Research News
New Bedford officer running 100 miles to fight fatal child disease
NEW BEDFORD — One hundred miles in one day. Not driving. Running. That is the goal that Stephen Taylor, 41, of New Bedford, has set for himself to raise awareness of a genetic disease that killed a colleague’s 2-year-old son last year. “I think I have the easy part,” he said. A resource police officer [...]
In: SMA Fund News, USA
Progress against genetic infant killer
SALT LAKE CITY, June 17 (UPI) — U.S. researchers report progress fighting spinal muscular atrophy, a genetic killer of infants and toddlers. Study leader Dr. Kathryn Swoboda of the University of Utah in Salt Lake City says researchers are making strides in understanding spinal muscular atrophy — a group of inherited diseases that cause progressive [...]
In: SMA Research News
Gwendolyn Strong Foundation Awards $10,000 To Critical SMA Online Support Network
The Gwendolyn Strong Foundation, a Santa Barbara, California based nonprofit organization dedicated to increasing awareness, research funding, and support for Spinal Muscular Atrophy (SMA), the #1 genetic killer of young children, has awarded a $10,000 grant to Eminnea, Inc., a Maryland based nonprofit organization, for its SMAspace.com project. SMAspace is a critical SMA online patient [...]
In: SMA Fund News, USA
New Novel Gene Treatment For Spinal Muscular Atrophy
Research that has just been published on the ninth of this month in Science Translation Medicine, has demonstrated that novel gene transfer system has the promise to furnish an efficient therapeutic treatment for SMA patients. Children who are currently enduring this disease are confirmed to prosper in this new ground breaking therapy developed by the [...]
In: SMA Research News
New therapy offers hope to spinal muscular atrophy patients
Children who suffer from the devastating disease Spinal Muscular Atrophy are set to benefit from a new breakthrough in therapy developments by researchers at the University of Sheffield. The research, which was published in Science Translational Medicine, has shown that a novel gene transfer system has the potential to provide an effective therapeutic treatment for [...]
In: SMA Research News
Fundraiser set for funeral of Murrieta girl who lost battle with rare illness
FUNDRAISER: The family of Aubrey Gross, a 6-month-old who died of a rare disorder, is raising money for funeral costs. WHEN: 2 p.m. Sunday WHERE: Aloha J’s restaurant, 27494 Ynez Road, Temecula DETAILS: The event will feature live music and costs a $5 donation. A weekend benefit in Temecula was planned to raise money so [...]
In: SMA Events, SMA Fund News, USA, USA
Stop SMA wins $250K contest in the Pepsi Refresh Project online contest in March
Stop SMA, a local nonprofit dedicated to raising money and awareness to educate the public about spinal muscular atrophy, won $250,000 in the Pepsi Refresh Project online contest in March. Jeff and Dee Horton, of Flowood, created the organization in honor of their daughter Evie, who has SMA. The money will go toward a coincidentally [...]
In: SMA Fund News, USA